| Name | Market Cap | Current Price | P/E Ratio | Revenue Growth 1Y | Net Margin | ROE | FCF Yield | Debt/Equity |
|---|---|---|---|---|---|---|---|---|
| KRYSKrystal Biotech, Inc. | 8.47B | 291.93 | 97.31 | 473.02% | 53.3% | 17.48% | 1.41% | 0.01 |
| BMRNBioMarin Pharmaceutical Inc. | 10.6B | 55.20 | 24.98 | 17.97% | 16.82% | 8.59% | 4.48% | 0.11 |
| SRPTSarepta Therapeutics, Inc. | 2.25B | 21.46 | 9.17 | 52.97% | -11.25% | -20.57% | 0.88 | |
| RAREUltragenyx Pharmaceutical Inc. | 2.33B | 24.11 | -3.83 | 29.01% | -91.95% | -35.88% | 0.15 | |
| DYNDyne Therapeutics, Inc. | 2.81B | 17.04 | -5.06 | -61.26% | 0.04 | |||
| TVTXTravere Therapeutics, Inc. | 2.6B | 29.11 | -7.13 | 60.55% | -20.32% | -120.36% | 6.80 | |
| BEAMBeam Therapeutics Inc. | 3.51B | 34.55 | -7.54 | -83.18% | -7.44% | -42.92% | 0.22 | |
| SLNOSoleno Therapeutics, Inc. | 2.23B | 41.51 | -9.48 | -79.5% | -15.85% | 0.22 |
| Dec 2015 | Dec 2016 | Dec 2017 | Dec 2018 | Dec 2019 | Dec 2020 | Dec 2021 | Dec 2022 | Dec 2023 | Dec 2024 | |
|---|---|---|---|---|---|---|---|---|---|---|
| Sales/Revenue | 0 | 0 | 0 | 3.5M | 0 | 3M | 0 | 0 | 0 | 2.56M |
| Revenue Growth % | - | - | - | - | -1% | - | -1% | - | - | - |
| Cost of Goods Sold | 400K | 300K | 195K | 103K | 672K | 0 | 0 | 0 | 0 | 797K |
| COGS % of Revenue | - | - | - | 0.03% | - | - | - | - | - | 0.31% |
| Gross Profit | -400K | -300K | -195K | 3.4M | -672K | 3M | 0 | 0 | 0 | 1.76M |
| Gross Margin % | - | - | - | 0.97% | - | 1% | - | - | - | 0.69% |
| Gross Profit Growth % | - | 0.25% | 0.35% | 18.42% | -1.2% | 5.46% | -1% | - | - | - |
| Operating Expenses | 12.67M | 21.96M | 32.27M | 46.21M | 47.8M | 62.87M | 85.11M | 87.57M | 107.52M | 38.16M |
| OpEx % of Revenue | - | - | - | 13.2% | - | 20.96% | - | - | - | 14.92% |
| Selling, General & Admin | 2.12M | 6.51M | 8.01M | 18.41M | 17.64M | 20.94M | 24.7M | 27.02M | 35.51M | 61.52M |
| SG&A % of Revenue | - | - | - | 5.26% | - | 6.98% | - | - | - | 24.06% |
| Research & Development | 12.71M | 17.83M | 28.13M | 30.98M | 30.16M | 41.93M | 50.65M | 61.06M | 72.02M | 81.64M |
| R&D % of Revenue | - | - | - | 8.85% | - | 13.98% | - | - | - | 31.93% |
| Other Operating Expenses | -77K | 104K | -16K | -85K | 0 | 0 | 9.76M | -509K | 0 | -105M |
| Operating Income | -14.82M | -24.35M | -36.13M | -45.88M | -51.7M | -59.87M | -85.11M | -87.57M | -107.52M | -36.4M |
| Operating Margin % | - | - | - | -13.11% | - | -19.96% | - | - | - | -14.24% |
| Operating Income Growth % | - | -0.64% | -0.48% | -0.27% | -0.13% | -0.16% | -0.42% | -0.03% | -0.23% | 0.66% |
| EBITDA | -14.44M | -24.05M | -35.94M | -45.78M | -51.03M | -58.64M | -84.61M | -87.06M | -107.1M | -35.6M |
| EBITDA Margin % | - | - | - | -13.08% | - | -19.55% | - | - | - | -13.92% |
| EBITDA Growth % | - | -0.67% | -0.49% | -0.27% | -0.11% | -0.15% | -0.44% | -0.03% | -0.23% | 0.67% |
| D&A (Non-Cash Add-back) | 389K | 300K | 195K | 103K | 672K | 1.23M | 499K | 513K | 419K | 796K |
| EBIT | -12.75M | -20.46M | -31.8M | -32.56M | -50.66M | -59.3M | -85.04M | -89.85M | -95.31M | -28.37M |
| Net Interest Income | 0 | 0 | -1.86M | -230K | -950K | -2.42M | -3.63M | -3.77M | -1.2M | -3M |
| Interest Income | 0 | 0 | 214K | 809K | 1.2M | 273K | 10K | 219K | 4.58M | 5.77M |
| Interest Expense | 472K | 2.52M | 2.08M | 1.04M | 2.15M | 2.69M | 3.64M | 3.99M | 5.78M | 8.77M |
| Other Income/Expense | 1.61M | 6.48M | 2.26M | 2.86M | -1.1M | -2.11M | -3.57M | -6.27M | 6.43M | -739K |
| Pretax Income | -13.22M | -22.98M | -33.88M | -43.02M | -52.81M | -61.98M | -88.68M | -93.84M | -101.09M | -37.14M |
| Pretax Margin % | - | - | - | -12.29% | - | -20.66% | - | - | - | -14.52% |
| Income Tax | 0 | 2.62M | 0 | 3.9M | 0 | 148K | 17K | 28K | 78K | 310K |
| Effective Tax Rate % | 1% | 1% | 1% | 1% | 1.07% | 1% | 1% | 1% | 1% | 1.01% |
| Net Income | -13.22M | -22.98M | -33.88M | -43.02M | -56.6M | -62.13M | -88.7M | -93.87M | -101.17M | -37.45M |
| Net Margin % | - | - | - | -12.29% | - | -20.71% | - | - | - | -14.65% |
| Net Income Growth % | - | -0.74% | -0.47% | -0.27% | -0.32% | -0.1% | -0.43% | -0.06% | -0.08% | 0.63% |
| Net Income (Continuing) | -13.22M | -22.98M | -33.88M | -33.28M | -52.81M | -62.13M | -88.7M | -93.87M | -101.17M | -37.45M |
| Discontinued Operations | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Minority Interest | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| EPS (Diluted) | -1000.15 | -1737.74 | -1637.10 | -2373.00 | -138.90 | -92.70 | -119.70 | -45.60 | -17.10 | -5.59 |
| EPS Growth % | - | -0.74% | 0.06% | -0.45% | 0.94% | 0.33% | -0.29% | 0.62% | 0.63% | 0.67% |
| EPS (Basic) | -1000.15 | -1737.74 | -1637.10 | -2373.00 | -138.90 | -92.70 | -119.70 | -45.60 | -17.10 | -5.59 |
| Diluted Shares Outstanding | 13.23K | 13.23K | 15.27K | 15.3K | 384.33K | 669.23K | 858.29K | 2.12M | 5.93M | 6.7M |
| Basic Shares Outstanding | 13.23K | 13.23K | 13.43K | 14.03K | 380.07K | 669.23K | 741.7K | 2.06M | 5.93M | 6.7M |
| Dividend Payout Ratio | - | - | - | - | - | - | - | - | - | - |
| Dec 2015 | Dec 2016 | Dec 2017 | Dec 2018 | Dec 2019 | Dec 2020 | Dec 2021 | Dec 2022 | Dec 2023 | Dec 2024 | |
|---|---|---|---|---|---|---|---|---|---|---|
| Total Current Assets | 8.39M | 5.72M | 80.83M | 35.08M | 129.28M | 83.31M | 87.88M | 128.68M | 122.08M | 112.17M |
| Cash & Short-Term Investments | 6.76M | 3.04M | 76.79M | 30.75M | 126.18M | 78.71M | 81.79M | 121.72M | 114.22M | 102.06M |
| Cash Only | 6.76M | 3.04M | 76.79M | 30.75M | 126.18M | 78.71M | 81.79M | 121.72M | 99.22M | 55.7M |
| Short-Term Investments | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 15M | 46.36M |
| Accounts Receivable | 1.54M | 1.34M | 1.61M | 2.86M | 2M | 917K | 747K | 1.15M | 562K | 1.71M |
| Days Sales Outstanding | - | - | - | 298.15 | - | 111.57 | - | - | - | 244.09 |
| Inventory | 0 | 1.25M | 355K | 0 | 0 | 0 | 0 | 0 | 0 | 2.82M |
| Days Inventory Outstanding | - | 1.52K | 664.49 | - | - | - | - | - | - | 1.29K |
| Other Current Assets | 0 | 0 | 0 | 101K | 0 | 0 | 0 | 5.81M | 7.3M | 5.59M |
| Total Non-Current Assets | 1.12M | 1.89M | 421K | 924K | 31.42M | 39.56M | 29.3M | 26.91M | 25.18M | 34.27M |
| Property, Plant & Equipment | 760K | 519K | 421K | 285K | 2.36M | 9.2M | 10.22M | 8.33M | 6.39M | 4.84M |
| Fixed Asset Turnover | - | - | - | 12.28x | - | 0.33x | - | - | - | 0.53x |
| Goodwill | 0 | 0 | 0 | 0 | 27.11M | 27.11M | 17.35M | 17.35M | 17.35M | 17.35M |
| Intangible Assets | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 10M |
| Long-Term Investments | 338K | 394K | 355K | 364K | 0 | 0 | 1.32M | 1.02M | 0 | 0 |
| Other Non-Current Assets | 25K | 975K | -355K | 275K | 1.95M | 3.26M | 1.72M | 1.23M | 1.44M | 2.08M |
| Total Assets | 9.51M | 7.6M | 81.25M | 36M | 160.7M | 122.87M | 117.18M | 155.59M | 147.26M | 146.45M |
| Asset Turnover | - | - | - | 0.10x | - | 0.02x | - | - | - | 0.02x |
| Asset Growth % | - | -0.2% | 9.69% | -0.56% | 3.46% | -0.24% | -0.05% | 0.33% | -0.05% | -0.01% |
| Total Current Liabilities | 6.68M | 12.06M | 7.68M | 5.4M | 9.45M | 11.95M | 14.02M | 22.32M | 22.86M | 32.88M |
| Accounts Payable | 423K | 1.65M | 1.89M | 545K | 2.09M | 3.14M | 4.28M | 7.78M | 8.95M | 8.62M |
| Days Payables Outstanding | 385.99 | 2K | 3.54K | 1.93K | 1.13K | - | - | - | - | 3.95K |
| Short-Term Debt | 2.49M | 5.13M | 2.31M | 1.69M | 0 | 0 | 795K | 1.31M | 0 | 0 |
| Deferred Revenue (Current) | 430K | 504K | 1000K | 737K | 0 | 0 | 0 | 0 | 0 | 0 |
| Other Current Liabilities | 2.39M | 3.48M | 3.33M | 1.5M | 2.92M | 3.76M | 5.42M | 6.59M | 8.2M | 13.05M |
| Current Ratio | 1.26x | 0.47x | 10.52x | 6.50x | 13.68x | 6.97x | 6.27x | 5.76x | 5.34x | 3.41x |
| Quick Ratio | 1.26x | 0.37x | 10.48x | 6.50x | 13.68x | 6.97x | 6.27x | 5.76x | 5.34x | 3.33x |
| Cash Conversion Cycle | - | - | - | - | - | - | - | - | - | -2.41K |
| Total Non-Current Liabilities | 37.16M | 52.11M | 14.87M | 9.01M | 22.03M | 38.12M | 38.74M | 59.21M | 73.3M | 91.42M |
| Long-Term Debt | 4.7M | 10.13M | 9.92M | 7.89M | 20.1M | 33.18M | 33.14M | 32.3M | 54.57M | 75.42M |
| Capital Lease Obligations | -29.95M | -39.84M | 0 | 0 | 1.92M | 4.48M | 4.78M | 3.6M | 2.61M | 1.41M |
| Deferred Tax Liabilities | 29.95M | 39.84M | -9K | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Other Non-Current Liabilities | -29.88M | -39.75M | 9K | 5K | 16K | 462K | 826K | 23.3M | 16.11M | 14.59M |
| Total Liabilities | 43.83M | 64.17M | 22.55M | 14.4M | 31.48M | 50.07M | 52.76M | 81.53M | 96.16M | 124.3M |
| Total Debt | 7.19M | 15.29M | 12.24M | 7.89M | 22.91M | 38.45M | 39.78M | 38.42M | 58.28M | 78.09M |
| Net Debt | 435K | 12.25M | -64.56M | -22.86M | -103.27M | -40.26M | -42M | -83.3M | -40.94M | 22.39M |
| Debt / Equity | - | - | 0.21x | 0.37x | 0.18x | 0.53x | 0.62x | 0.52x | 1.14x | 3.53x |
| Debt / EBITDA | - | - | - | - | - | - | - | - | - | - |
| Net Debt / EBITDA | - | - | - | - | - | - | - | - | - | - |
| Interest Coverage | -31.41x | -9.68x | -17.38x | -44.16x | -24.08x | -22.27x | -23.37x | -21.93x | -18.61x | -4.15x |
| Total Equity | -34.32M | -56.56M | 58.71M | 21.6M | 129.22M | 72.8M | 64.41M | 74.05M | 51.1M | 22.15M |
| Equity Growth % | - | -0.65% | 2.04% | -0.63% | 4.98% | -0.44% | -0.12% | 0.15% | -0.31% | -0.57% |
| Book Value per Share | -2593.28 | -4273.67 | 3845.44 | 1411.77 | 336.22 | 108.78 | 75.05 | 34.97 | 8.62 | 3.30 |
| Total Shareholders' Equity | -34.32M | -56.56M | 58.71M | 21.6M | 129.22M | 72.8M | 64.41M | 74.05M | 51.1M | 22.15M |
| Common Stock | 1K | 1K | 15K | 15K | 16K | 16K | 28K | 122K | 167K | 171K |
| Retained Earnings | -35.41M | -58.39M | -92.27M | -135.29M | -132.04M | -194.18M | -282.87M | -376.74M | -477.9M | -515.36M |
| Treasury Stock | -371K | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Accumulated OCI | 718K | 834K | 127K | 241K | -119K | -119K | -119K | -119K | -119K | -122K |
| Minority Interest | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Dec 2015 | Dec 2016 | Dec 2017 | Dec 2018 | Dec 2019 | Dec 2020 | Dec 2021 | Dec 2022 | Dec 2023 | Dec 2024 | |
|---|---|---|---|---|---|---|---|---|---|---|
| Cash from Operations | -10.82M | -21.64M | -27.87M | -40.9M | -48.05M | -58.82M | -70.91M | -77.1M | -96.51M | -130.9M |
| Operating CF Margin % | - | - | - | -11.69% | - | -19.61% | - | - | - | -51.19% |
| Operating CF Growth % | - | -1% | -0.29% | -0.47% | -0.17% | -0.22% | -0.21% | -0.09% | -0.25% | -0.36% |
| Net Income | -13.22M | -22.98M | -33.88M | -43.02M | -52.81M | -62.13M | -88.7M | -93.87M | -101.17M | -37.45M |
| Depreciation & Amortization | 389K | 285K | 195K | 155K | 103K | 351K | 499K | 513K | 419K | 796K |
| Stock-Based Compensation | 126K | 644K | 906K | 5.62M | 2.05M | 5.43M | 6.18M | 5.2M | 8.69M | 8.2M |
| Deferred Taxes | -1K | -1.39M | -269K | 0 | -2.15M | -5.78M | -6.68M | 0 | 0 | 0 |
| Other Non-Cash Items | 441K | 2.32M | 1.75M | 804K | 7.99M | 7.38M | 19.29M | 5.32M | -4.79M | -105.13M |
| Working Capital Changes | 1.45M | -517K | 3.42M | -4.46M | -3.24M | -4.06M | -1.5M | 5.74M | 344K | 2.67M |
| Change in Receivables | -56K | 152K | -64K | -1.37M | 0 | 0 | 0 | -610K | 0 | -1.07M |
| Change in Inventory | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 610K | 0 | -2.82M |
| Change in Payables | 77K | 1.26M | 182K | -1.34M | -2.75M | 1.03M | 1.17M | 3.42M | 1.23M | -286K |
| Cash from Investing | -247K | -138K | 34K | -34K | 27.23M | -1.36M | -615K | -103K | -14.88M | 66.99M |
| Capital Expenditures | -170K | -73K | -42K | -34K | -174K | -1.36M | -615K | -103K | -60K | -326K |
| CapEx % of Revenue | - | - | - | 0.01% | - | 0.45% | - | - | - | 0.13% |
| Acquisitions | - | - | - | - | - | - | - | - | - | - |
| Investments | - | - | - | - | - | - | - | - | - | - |
| Other Investing | -77K | -65K | 76K | 0 | 1M | 0 | 0 | 4.8M | 0 | 98M |
| Cash from Financing | 11.51M | 18.15M | 101.26M | -4.53M | 140.66M | 12.39M | 74.25M | 117.23M | 88.52M | 20.29M |
| Debt Issued (Net) | - | - | - | - | - | - | - | - | - | - |
| Equity Issued (Net) | - | - | - | - | - | - | - | - | - | - |
| Dividends Paid | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Share Repurchases | - | - | - | - | - | - | - | - | - | - |
| Other Financing | 16K | -30K | -7.87M | 7K | 792K | 284K | 260K | -4.61M | 8.08M | 0 |
| Net Change in Cash | - | - | - | - | - | - | - | - | - | - |
| Free Cash Flow | -10.99M | -21.71M | -27.91M | -40.94M | -48.23M | -60.18M | -71.52M | -77.2M | -96.57M | -131.23M |
| FCF Margin % | - | - | - | -11.7% | - | -20.06% | - | - | - | -51.32% |
| FCF Growth % | - | -0.98% | -0.29% | -0.47% | -0.18% | -0.25% | -0.19% | -0.08% | -0.25% | -0.36% |
| FCF per Share | -830.07 | -1640.50 | -1828.36 | -2675.62 | -125.49 | -89.92 | -83.33 | -36.46 | -16.29 | -19.58 |
| FCF Conversion (FCF/Net Income) | 0.82x | 0.94x | 0.82x | 0.95x | 0.85x | 0.95x | 0.80x | 0.82x | 0.95x | 3.50x |
| Interest Paid | 81K | 291K | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Taxes Paid | 29K | 4K | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Metric | 2015 | 2016 | 2017 | 2018 | 2019 | 2020 | 2021 | 2022 | 2023 | 2024 |
|---|---|---|---|---|---|---|---|---|---|---|
| Return on Equity (ROE) | - | - | -3158.69% | -107.14% | -75.06% | -61.51% | -129.28% | -135.58% | -161.67% | -102.26% |
| Return on Invested Capital (ROIC) | - | - | - | - | -314.13% | -153.55% | -232.33% | -997.9% | -17588.11% | -99.82% |
| Gross Margin | - | - | - | 97.06% | - | 100% | - | - | - | 68.83% |
| Net Margin | - | - | - | -1229.17% | - | -2071.03% | - | - | - | -1464.61% |
| Debt / Equity | - | - | 0.21x | 0.37x | 0.18x | 0.53x | 0.62x | 0.52x | 1.14x | 3.53x |
| Interest Coverage | -31.41x | -9.68x | -17.38x | -44.16x | -24.08x | -22.27x | -23.37x | -21.93x | -18.61x | -4.15x |
| FCF Conversion | 0.82x | 0.94x | 0.82x | 0.95x | 0.85x | 0.95x | 0.80x | 0.82x | 0.95x | 3.50x |
| Revenue Growth | - | - | - | - | -100% | - | -100% | - | - | - |
| 2024 | |
|---|---|
| Product Returns | 11K |
| Product Returns Growth | - |
X4 Pharmaceuticals, Inc. (XFOR) reported $34.0M in revenue for fiscal year 2024.
X4 Pharmaceuticals, Inc. (XFOR) grew revenue by 0.0% over the past year. Growth has been modest.
X4 Pharmaceuticals, Inc. (XFOR) reported a net loss of $95.1M for fiscal year 2024.
X4 Pharmaceuticals, Inc. (XFOR) has a return on equity (ROE) of -102.3%. Negative ROE indicates the company is unprofitable.
X4 Pharmaceuticals, Inc. (XFOR) had negative free cash flow of $106.1M in fiscal year 2024, likely due to heavy capital investments.