| Name | Market Cap | Current Price | P/E Ratio | Revenue Growth 1Y | Net Margin | ROE | FCF Yield | Debt/Equity |
|---|---|---|---|---|---|---|---|---|
| KRYSKrystal Biotech, Inc. | 8.18B | 282.01 | 94.00 | 473.02% | 53.3% | 17.48% | 1.46% | 0.01 |
| BMRNBioMarin Pharmaceutical Inc. | 10.58B | 55.07 | 24.92 | 17.97% | 16.82% | 8.59% | 4.49% | 0.11 |
| SRPTSarepta Therapeutics, Inc. | 2.23B | 21.31 | 9.11 | 52.97% | -11.25% | -20.57% | 0.88 | |
| RAREUltragenyx Pharmaceutical Inc. | 2.27B | 23.50 | -3.74 | 29.01% | -91.95% | -35.88% | 0.15 | |
| DYNDyne Therapeutics, Inc. | 2.7B | 16.42 | -4.87 | -61.26% | 0.04 | |||
| TVTXTravere Therapeutics, Inc. | 2.54B | 28.40 | -6.96 | 60.55% | -20.32% | -120.36% | 6.80 | |
| BEAMBeam Therapeutics Inc. | 3.25B | 32.05 | -7.00 | -83.18% | -7.44% | -42.92% | 0.22 | |
| SLNOSoleno Therapeutics, Inc. | 2.25B | 41.95 | -9.58 | -79.5% | -15.85% | 0.22 |
| Dec 2015 | Dec 2016 | Dec 2017 | Dec 2018 | Dec 2019 | Dec 2020 | Dec 2021 | Dec 2022 | Dec 2023 | Dec 2024 | |
|---|---|---|---|---|---|---|---|---|---|---|
| Sales/Revenue | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Revenue Growth % | - | - | - | - | - | - | - | - | - | - |
| Cost of Goods Sold | 45K | 169K | 204K | 330K | 426K | 1.15M | 0 | 0 | 0 | 0 |
| COGS % of Revenue | - | - | - | - | - | - | - | - | - | - |
| Gross Profit | -45K | -169K | -204K | -330K | -426K | -1.15M | 0 | 0 | 0 | 0 |
| Gross Margin % | - | - | - | - | - | - | - | - | - | - |
| Gross Profit Growth % | - | -2.76% | -0.21% | -0.62% | -0.29% | -1.69% | 1% | - | - | - |
| Operating Expenses | 20.4M | 41.88M | 26.74M | 70.97M | 75.9M | 134.86M | 167.25M | 224.34M | 259.66M | 273.2M |
| OpEx % of Revenue | - | - | - | - | - | - | - | - | - | - |
| Selling, General & Admin | 7.84M | 9.89M | 12.54M | 17.89M | 17.53M | 27.92M | 41.77M | 58.77M | 73.32M | 101.96M |
| SG&A % of Revenue | - | - | - | - | - | - | - | - | - | - |
| Research & Development | 12.55M | 31.98M | 14.19M | 53.27M | 58.62M | 106.38M | 125.48M | 165.57M | 186.34M | 171.24M |
| R&D % of Revenue | - | - | - | - | - | - | - | - | - | - |
| Other Operating Expenses | 0 | 0 | 0 | -186K | -250K | 0 | 0 | 0 | 0 | 0 |
| Operating Income | -20.4M | -41.88M | -26.74M | -71.16M | -76.15M | -136M | -167.25M | -224.34M | -259.66M | -273.2M |
| Operating Margin % | - | - | - | - | - | - | - | - | - | - |
| Operating Income Growth % | -1.65% | -1.05% | 0.36% | -1.66% | -0.07% | -0.79% | -0.23% | -0.34% | -0.16% | -0.05% |
| EBITDA | -20.35M | -41.71M | -26.53M | -70.83M | -75.72M | -134.86M | -161.88M | -218.08M | -252.56M | -263.83M |
| EBITDA Margin % | - | - | - | - | - | - | - | - | - | - |
| EBITDA Growth % | -1.64% | -1.05% | 0.36% | -1.67% | -0.07% | -0.78% | -0.2% | -0.35% | -0.16% | -0.04% |
| D&A (Non-Cash Add-back) | 45K | 169K | 204K | 330K | 426K | 1.15M | 5.37M | 6.27M | 7.1M | 9.38M |
| EBIT | -66.75M | -41.44M | -20.21M | -68.67M | -71.56M | -132.73M | -163.18M | -219.95M | -243.72M | -256.86M |
| Net Interest Income | -1.14M | -975K | -2.76M | -3.55M | -1.37M | -5.4M | -2.82M | 1.98M | 14.06M | 16.34M |
| Interest Income | 89K | 443K | 819K | 1.69M | 3.41M | 2.15M | 3.07M | 3.89M | 15.94M | 18.22M |
| Interest Expense | 1.23M | 1.42M | 3.58M | 5.24M | 4.78M | 7.55M | 5.89M | 1.91M | 1.88M | 1.89M |
| Other Income/Expense | -47.59M | -975K | -2.76M | -3.36M | -1.12M | -3.7M | -1.82M | 2.48M | 14.06M | 14.46M |
| Pretax Income | -67.98M | -42.85M | -29.5M | -74.52M | -77.27M | -139.7M | -169.07M | -221.86M | -245.59M | -258.75M |
| Pretax Margin % | - | - | - | - | - | - | - | - | - | - |
| Income Tax | 0 | 0 | 0 | 0 | 0 | 6.97M | 0 | 0 | 0 | 0 |
| Effective Tax Rate % | 1% | 1% | 1% | 1% | 1.08% | 1.05% | 1% | 1% | 1% | 1% |
| Net Income | -67.98M | -42.85M | -29.5M | -74.52M | -83.23M | -146.67M | -169.07M | -221.86M | -245.59M | -258.75M |
| Net Margin % | - | - | - | - | - | - | - | - | - | - |
| Net Income Growth % | -6.13% | 0.37% | 0.31% | -1.53% | -0.12% | -0.76% | -0.15% | -0.31% | -0.11% | -0.05% |
| Net Income (Continuing) | -67.98M | -42.85M | -29.5M | -74.52M | -77.27M | -146.67M | -169.07M | -221.86M | -245.59M | -258.75M |
| Discontinued Operations | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Minority Interest | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| EPS (Diluted) | -14.85 | -6.41 | -4.36 | -1.89 | -1.70 | -2.52 | -2.68 | -3.26 | -2.92 | -2.73 |
| EPS Growth % | -2.28% | 0.57% | 0.32% | 0.57% | 0.1% | -0.48% | -0.06% | -0.22% | 0.1% | 0.07% |
| EPS (Basic) | -10.29 | -6.41 | -4.36 | -1.89 | -1.70 | -2.52 | -2.68 | -3.26 | -2.92 | -2.73 |
| Diluted Shares Outstanding | 6.61M | 6.68M | 6.77M | 39.38M | 49.01M | 55.38M | 63.24M | 68.15M | 84.01M | 94.81M |
| Basic Shares Outstanding | 6.61M | 6.68M | 6.77M | 39.38M | 49.01M | 55.38M | 63.24M | 68.15M | 84.01M | 94.81M |
| Dividend Payout Ratio | - | - | - | - | - | - | - | - | - | - |
| Dec 2015 | Dec 2016 | Dec 2017 | Dec 2018 | Dec 2019 | Dec 2020 | Dec 2021 | Dec 2022 | Dec 2023 | Dec 2024 | |
|---|---|---|---|---|---|---|---|---|---|---|
| Total Current Assets | 112.37M | 128.35M | 101.05M | 209.09M | 307.75M | 487.35M | 392.06M | 364.06M | 378.22M | 378.18M |
| Cash & Short-Term Investments | 111.28M | 126.47M | 100.01M | 205.73M | 304.12M | 482.72M | 388.74M | 356.39M | 373.18M | 372.34M |
| Cash Only | 80.04M | 29.8M | 78.72M | 111.36M | 185.38M | 297.1M | 232.69M | 140.52M | 55.9M | 163.63M |
| Short-Term Investments | 31.24M | 96.67M | 21.29M | 94.38M | 118.73M | 185.62M | 156.05M | 215.88M | 317.27M | 208.7M |
| Accounts Receivable | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Days Sales Outstanding | - | - | - | - | - | - | - | - | - | - |
| Inventory | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Days Inventory Outstanding | - | - | - | - | - | - | - | - | - | - |
| Other Current Assets | 0 | 0 | 0 | 3.36M | 0 | 0 | 0 | 7.67M | 5.05M | 5.85M |
| Total Non-Current Assets | 955K | 1.3M | 731K | 42.23M | 64.37M | 103.48M | 104.96M | 187.75M | 188.12M | 149.52M |
| Property, Plant & Equipment | 812K | 1.13M | 563K | 2.03M | 31.35M | 70.64M | 72.35M | 77.64M | 87.59M | 83.32M |
| Fixed Asset Turnover | - | - | - | - | - | - | - | - | - | - |
| Goodwill | 0 | 0 | 0 | 30.82M | 30.82M | 30.82M | 30.82M | 39.15M | 39.15M | 39.15M |
| Intangible Assets | 0 | 0 | 0 | 0 | 226K | 0 | 0 | 25.72M | 25.15M | 25.15M |
| Long-Term Investments | 0 | 0 | 207K | 7.4M | 1.52M | 0 | 0 | 43.28M | 34.32M | 0 |
| Other Non-Current Assets | 143K | 168K | -39K | 1.44M | 1.98M | 3.59M | 1.8M | 1.95M | 1.91M | 1.89M |
| Total Assets | 113.32M | 129.65M | 101.78M | 251.31M | 372.12M | 590.82M | 497.02M | 551.81M | 566.34M | 527.7M |
| Asset Turnover | - | - | - | - | - | - | - | - | - | - |
| Asset Growth % | 19.53% | 0.14% | -0.21% | 1.47% | 0.48% | 0.59% | -0.16% | 0.11% | 0.03% | -0.07% |
| Total Current Liabilities | 4.14M | 7.21M | 4.07M | 15.37M | 18.31M | 32.62M | 22.17M | 39.17M | 48.51M | 40.68M |
| Accounts Payable | 1.63M | 1.59M | 451K | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Days Payables Outstanding | 13.25K | 3.44K | 806.94 | - | - | - | - | - | - | - |
| Short-Term Debt | 0 | 0 | 0 | 0 | 957K | 4.88M | 0 | 0 | 0 | 0 |
| Deferred Revenue (Current) | 450K | 478K | 506K | 534K | 562K | 590K | 0 | 0 | 0 | 0 |
| Other Current Liabilities | 549K | 2.97M | 557K | 12.93M | 12.68M | 2M | 4.53M | 10.01M | 9.93M | 11.94M |
| Current Ratio | 27.13x | 17.80x | 24.83x | 13.60x | 16.81x | 14.94x | 17.69x | 9.29x | 7.80x | 9.30x |
| Quick Ratio | 27.13x | 17.80x | 24.83x | 13.60x | 16.81x | 14.94x | 17.69x | 9.29x | 7.80x | 9.30x |
| Cash Conversion Cycle | - | - | - | - | - | - | - | - | - | - |
| Total Non-Current Liabilities | 367K | 49.27M | 49.94M | 41.9M | 46.52M | 54.69M | 20.13M | 22.95M | 25.26M | 23.78M |
| Long-Term Debt | 0 | 48.96M | 49.54M | 41.45M | 45.05M | 35.07M | 0 | 0 | 0 | 0 |
| Capital Lease Obligations | 0 | 0 | 0 | 0 | 1.44M | 19.49M | 20.05M | 20.36M | 22.33M | 22.64M |
| Deferred Tax Liabilities | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Other Non-Current Liabilities | 367K | 307K | 403K | 457K | 23K | 136K | 80K | 2.6M | 2.94M | 1.14M |
| Total Liabilities | 4.51M | 56.48M | 54.01M | 57.28M | 64.82M | 87.31M | 42.3M | 62.12M | 73.77M | 64.47M |
| Total Debt | 0 | 48.96M | 49.54M | 41.45M | 47.45M | 61.7M | 22.6M | 22.87M | 25.04M | 25.5M |
| Net Debt | -80.04M | 19.16M | -29.18M | -69.91M | -137.93M | -235.4M | -210.09M | -117.65M | -30.86M | -138.14M |
| Debt / Equity | - | 0.67x | 1.04x | 0.21x | 0.15x | 0.12x | 0.05x | 0.05x | 0.05x | 0.06x |
| Debt / EBITDA | - | - | - | - | - | - | - | - | - | - |
| Net Debt / EBITDA | - | - | - | - | - | - | - | - | - | - |
| Interest Coverage | -16.58x | -29.53x | -7.47x | -13.58x | -15.92x | -18.02x | -28.40x | -117.52x | -138.48x | -144.86x |
| Total Equity | 108.81M | 73.17M | 47.76M | 194.04M | 307.3M | 503.52M | 454.72M | 489.69M | 492.57M | 463.23M |
| Equity Growth % | 3.11% | -0.33% | -0.35% | 3.06% | 0.58% | 0.64% | -0.1% | 0.08% | 0.01% | -0.06% |
| Book Value per Share | 16.47 | 10.95 | 7.06 | 4.93 | 6.27 | 9.09 | 7.19 | 7.19 | 5.86 | 4.89 |
| Total Shareholders' Equity | 108.81M | 73.17M | 47.76M | 194.04M | 307.3M | 503.52M | 454.72M | 489.69M | 492.57M | 463.23M |
| Common Stock | 264K | 270K | 68K | 452K | 548K | 610K | 645K | 791K | 903K | 1.06M |
| Retained Earnings | -196.02M | -238.88M | -268.37M | -105.87M | -183.14M | -322.84M | -491.91M | -713.77M | -959.37M | -1.22B |
| Treasury Stock | 0 | 0 | 263.94M | -668K | -53K | 0 | 0 | -47K | 0 | 0 |
| Accumulated OCI | -11K | -54K | -16K | -127K | 20K | -42K | -161K | -357K | 319K | 66K |
| Minority Interest | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Dec 2015 | Dec 2016 | Dec 2017 | Dec 2018 | Dec 2019 | Dec 2020 | Dec 2021 | Dec 2022 | Dec 2023 | Dec 2024 | |
|---|---|---|---|---|---|---|---|---|---|---|
| Cash from Operations | -17.42M | -37.27M | -26.11M | -53.79M | -64.66M | -74.64M | -121.16M | -178.14M | -194.92M | -209.72M |
| Operating CF Margin % | - | - | - | - | - | - | - | - | - | - |
| Operating CF Growth % | -0.79% | -1.14% | 0.3% | -1.06% | -0.2% | -0.15% | -0.62% | -0.47% | -0.09% | -0.08% |
| Net Income | -67.98M | -42.85M | -29.5M | -74.52M | -77.27M | -139.7M | -169.07M | -221.86M | -245.59M | -258.75M |
| Depreciation & Amortization | 45K | 169K | 200K | 330K | 426K | 1.15M | 5.37M | 6.27M | 7.1M | 9.38M |
| Stock-Based Compensation | 2.38M | 2.91M | 4.04M | 13.6M | 13.37M | 18.57M | 29.24M | 31.01M | 39.41M | 43.92M |
| Deferred Taxes | 46.36M | 225K | 654K | -484K | -1.07M | 999K | 3.15M | 0 | 0 | 0 |
| Other Non-Cash Items | 1.11M | 162K | 522K | 2.9M | 3.6M | 29.32M | 13.53M | 370K | -9.28M | -6.19M |
| Working Capital Changes | 669K | 2.12M | -2.03M | 4.38M | -3.73M | 15.03M | -3.39M | 6.08M | 13.46M | 1.92M |
| Change in Receivables | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Change in Inventory | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Change in Payables | 487K | -41K | -1.14M | 5.89M | -2.72M | 11.02M | -4.83M | 9.67M | 0 | 0 |
| Cash from Investing | -31.68M | -66.06M | 75.02M | -5.27M | -39.01M | -96.59M | 18.85M | -69.33M | -98.07M | 131.71M |
| Capital Expenditures | -412K | -487K | -70K | -1.45M | -23.27M | -29.06M | -7.71M | -8.62M | -16.47M | -5.86M |
| CapEx % of Revenue | - | - | - | - | - | - | - | - | - | - |
| Acquisitions | - | - | - | - | - | - | - | - | - | - |
| Investments | - | - | - | - | - | - | - | - | - | - |
| Other Investing | 0 | 0 | 0 | -356K | -15.74K | -8.45M | -95K | 0 | 0 | 0 |
| Cash from Financing | 125.52M | 16 | 25.41K | 153.5M | 177.79M | 282.99M | 37.68M | 155.29M | 208.4M | 185.74M |
| Debt Issued (Net) | - | - | - | - | - | - | - | - | - | - |
| Equity Issued (Net) | - | - | - | - | - | - | - | - | - | - |
| Dividends Paid | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Share Repurchases | - | - | - | - | - | - | - | - | - | - |
| Other Financing | 106K | 346K | 19K | 148K | -313K | -3.85M | -201K | -172K | -132K | 0 |
| Net Change in Cash | - | - | - | - | - | - | - | - | - | - |
| Free Cash Flow | -17.83M | -37.75M | -26.18M | -55.24M | -87.93M | -103.7M | -128.88M | -186.76M | -211.39M | -215.59M |
| FCF Margin % | - | - | - | - | - | - | - | - | - | - |
| FCF Growth % | -0.83% | -1.12% | 0.31% | -1.11% | -0.59% | -0.18% | -0.24% | -0.45% | -0.13% | -0.02% |
| FCF per Share | -2.70 | -5.65 | -3.87 | -1.40 | -1.79 | -1.87 | -2.04 | -2.74 | -2.52 | -2.27 |
| FCF Conversion (FCF/Net Income) | 0.26x | 0.87x | 0.89x | 0.72x | 0.78x | 0.51x | 0.72x | 0.80x | 0.79x | 0.81x |
| Interest Paid | 0 | 0 | 0 | 4.49M | 2.99M | 0 | 0 | 0 | 0 | 0 |
| Taxes Paid | 0 | 0 | 0 | 2K | 26K | 0 | 0 | 0 | 0 | 0 |
| Metric | 2015 | 2016 | 2017 | 2018 | 2019 | 2020 | 2021 | 2022 | 2023 | 2024 |
|---|---|---|---|---|---|---|---|---|---|---|
| Return on Equity (ROE) | -237.48% | -47.1% | -48.78% | -61.64% | -33.2% | -36.18% | -35.29% | -46.98% | -50.01% | -54.14% |
| Return on Invested Capital (ROIC) | - | -51.87% | -36.16% | -74.79% | -38.92% | -46.63% | -48.93% | -54.57% | -46.72% | -52.08% |
| Debt / Equity | - | 0.67x | 1.04x | 0.21x | 0.15x | 0.12x | 0.05x | 0.05x | 0.05x | 0.06x |
| Interest Coverage | -16.58x | -29.53x | -7.47x | -13.58x | -15.92x | -18.02x | -28.40x | -117.52x | -138.48x | -144.86x |
| FCF Conversion | 0.26x | 0.87x | 0.89x | 0.72x | 0.78x | 0.51x | 0.72x | 0.80x | 0.79x | 0.81x |
Rocket Pharmaceuticals, Inc. (RCKT) grew revenue by 0.0% over the past year. Growth has been modest.
Rocket Pharmaceuticals, Inc. (RCKT) reported a net loss of $240.9M for fiscal year 2024.
Rocket Pharmaceuticals, Inc. (RCKT) has a return on equity (ROE) of -54.1%. Negative ROE indicates the company is unprofitable.
Rocket Pharmaceuticals, Inc. (RCKT) had negative free cash flow of $202.8M in fiscal year 2024, likely due to heavy capital investments.