| Name | Market Cap | Current Price | P/E Ratio | Revenue Growth 1Y | Net Margin | ROE | FCF Yield | Debt/Equity |
|---|---|---|---|---|---|---|---|---|
| CORTCorcept Therapeutics Incorporated | 3.78B | 35.70 | 43.54 | 12.79% | 13.01% | 15.3% | 3.75% | 0.01 |
| BMRNBioMarin Pharmaceutical Inc. | 11.86B | 61.73 | 34.29 | 10.83% | 5.73% | 6.11% | 0.10 | |
| VRTXVertex Pharmaceuticals Incorporated | 126.19B | 496.83 | 32.43 | 8.9% | 31.35% | 21.22% | 2.53% | 0.20 |
| CPRXCatalyst Pharmaceuticals, Inc. | 2.83B | 23.08 | 13.74 | 19.78% | 36.39% | 22.46% | 7.38% | 0.00 |
| HRMYHarmony Biosciences Holdings, Inc. | 1.65B | 28.54 | 10.53 | 21.51% | 18.27% | 18.24% | 21.12% | 0.02 |
| PTCTPTC Therapeutics, Inc. | 5.45B | 68.19 | 8.76 | 114.51% | 42.25% | |||
| BCRXBioCryst Pharmaceuticals, Inc. | 1.86B | 8.75 | 7.23 | 94.1% | 30.16% | 18.63% | ||
| RAREUltragenyx Pharmaceutical Inc. | 2.26B | 23.39 | -3.72 | 29.01% | -91.95% | -35.88% | 0.15 |
Analyze head-to-head performance against top industry competitors across valuation, growth, and profitability metrics.
| Dec 2016 | Dec 2017 | Dec 2018 | Dec 2019 | Dec 2020 | Dec 2021 | Dec 2022 | Dec 2023 | Dec 2024 | Sep 2025 | |
|---|---|---|---|---|---|---|---|---|---|---|
| Sales/Revenue | 1.12B | 1.31B | 1.49B | 1.7B | 1.86B | 1.85B | 2.1B | 2.42B | 2.85B | 0 |
| Revenue Growth % | 25.5% | 17.62% | 13.52% | 14.27% | 9.18% | -0.76% | 13.53% | 15.42% | 17.97% | -100% |
| Cost of Goods Sold | 209.62M | 241.79M | 315.26M | 359.47M | 524.27M | 470.51M | 503.02M | 532.06M | 580.24M | 0 |
| COGS % of Revenue | 18.77% | 18.41% | 21.14% | 21.09% | 28.18% | 25.48% | 24% | 21.99% | 20.33% | - |
| Gross Profit | 907.23M | 1.07B | 1.18B | 1.34B | 1.34B | 1.38B | 1.59B | 1.89B | 2.27B | 0 |
| Gross Margin % | 81.23% | 81.59% | 78.86% | 78.91% | 71.82% | 74.52% | 76% | 78.01% | 79.67% | - |
| Gross Profit Growth % | 22.95% | 18.15% | 9.72% | 14.34% | -0.62% | 2.96% | 15.79% | 18.46% | 20.48% | -100% |
| Operating Expenses | 1.71B | 1.09B | 1.3B | 1.45B | 1.38B | 1.46B | 1.43B | 1.7B | 1.79B | 0 |
| OpEx % of Revenue | 153.17% | 82.71% | 87.14% | 84.8% | 74.16% | 78.98% | 68.32% | 70.33% | 62.7% | - |
| Selling, General & Admin | 476.59M | 554.34M | 604.4M | 680.9M | 737.7M | 759.4M | 823.2M | 892.4M | 1.01B | 0 |
| SG&A % of Revenue | 42.67% | 42.2% | 40.53% | 39.96% | 39.65% | 41.13% | 39.27% | 36.89% | 35.35% | - |
| Research & Development | 661.9M | 610.75M | 696.33M | 715.01M | 628.12M | 628.79M | 649.61M | 746.77M | 747.18M | 0 |
| R&D % of Revenue | 59.27% | 46.49% | 46.69% | 41.96% | 33.76% | 34.06% | 30.99% | 30.87% | 26.18% | - |
| Other Operating Expenses | 572.16M | -78.53M | -1.21M | 49.13M | 13.81M | 69.91M | -40.76M | 62.22M | 33.28M | 0 |
| Operating Income | -803.43M | -14.7M | -123.52M | -100.46M | -43.44M | -82.34M | 160.97M | 185.77M | 484.21M | 0 |
| Operating Margin % | -71.94% | -1.12% | -8.28% | -5.9% | -2.33% | -4.46% | 7.68% | 7.68% | 16.97% | - |
| Operating Income Growth % | -625.76% | 98.17% | -740.3% | 18.67% | 56.76% | -89.55% | 295.5% | 15.41% | 160.65% | -100% |
| EBITDA | -706.52M | 73.16M | -27.85M | 4.84M | 61.73M | 25.7M | 262.94M | 290.16M | 580.64M | 0 |
| EBITDA Margin % | -63.26% | 5.57% | -1.87% | 0.28% | 3.32% | 1.39% | 12.54% | 11.99% | 20.35% | - |
| EBITDA Growth % | -1012.36% | 110.36% | -138.07% | 117.39% | 1174.66% | -58.37% | 923.2% | 10.35% | 100.11% | -100% |
| D&A (Non-Cash Add-back) | 96.91M | 87.86M | 95.67M | 105.3M | 105.17M | 108.04M | 101.97M | 104.39M | 96.43M | 0 |
| EBIT | -794.92M | 3.11M | -99.04M | -73.38M | -21.52M | -60.61M | 163.39M | 202.39M | 554.1M | 0 |
| Net Interest Income | -32.01M | -27.85M | -20.83M | -712K | -12.7M | -4.86M | 2.06M | 41M | 62.15M | 0 |
| Interest Income | 7.49M | 14.85M | 22.83M | 22.75M | 16.61M | 10.48M | 18.03M | 58.34M | 74.88M | 0 |
| Interest Expense | 39.5M | 42.71M | 43.66M | 23.46M | 29.31M | 15.34M | 15.97M | 17.34M | 12.67M | 0 |
| Other Income/Expense | -27.62M | -21.18M | -19.18M | 5.65M | -5.56M | 6.99M | -11.4M | 2.79M | 57.55M | 0 |
| Pretax Income | -831.05M | -35.88M | -142.71M | -94.81M | -49M | -75.35M | 149.58M | 188.56M | 541.76M | 26.79M |
| Pretax Margin % | -74.41% | -2.73% | -9.57% | -5.56% | -2.63% | -4.08% | 7.14% | 7.79% | 18.98% | - |
| Income Tax | -200.84M | 81.17M | -65.49M | -70.96M | -903.03M | -11.27M | 8.02M | 20.92M | 114.9M | 0 |
| Effective Tax Rate % | 75.83% | 326.25% | 54.11% | 25.15% | -1743.02% | 85.04% | 94.64% | 88.91% | 78.79% | 100% |
| Net Income | -630.21M | -117.04M | -77.21M | -23.85M | 854.03M | -64.08M | 141.56M | 167.65M | 426.86M | 26.79M |
| Net Margin % | -56.43% | -8.91% | -5.18% | -1.4% | 45.9% | -3.47% | 6.75% | 6.93% | 14.96% | - |
| Net Income Growth % | -266.83% | 81.43% | 34.03% | 69.11% | 3681.13% | -107.5% | 320.91% | 18.43% | 154.62% | -93.73% |
| Net Income (Continuing) | -630.21M | -117.04M | -77.21M | -23.85M | 854.03M | -64.08M | 141.56M | 167.65M | 426.86M | 0 |
| Discontinued Operations | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Minority Interest | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| EPS (Diluted) | -3.79 | -0.67 | -0.44 | -0.13 | 4.53 | -0.35 | 0.75 | 0.88 | 2.21 | 0.14 |
| EPS Growth % | -254.21% | 82.32% | 34.33% | 70.45% | 3584.62% | -107.73% | 314.29% | 17.33% | 151.14% | -93.67% |
| EPS (Basic) | -3.80 | -0.67 | -0.44 | -0.13 | 4.75 | -0.35 | 0.76 | 0.89 | 2.25 | 0.14 |
| Diluted Shares Outstanding | 166.22M | 174.43M | 177.27M | 179.04M | 191.68M | 182.85M | 188.96M | 191.59M | 196.71M | 191.64M |
| Basic Shares Outstanding | 165.99M | 174.43M | 177.06M | 179.04M | 180.8M | 182.85M | 185.27M | 187.83M | 190.03M | 191.64M |
| Dividend Payout Ratio | - | - | - | - | - | - | - | - | - | - |
| Dec 2016 | Dec 2017 | Dec 2018 | Dec 2019 | Dec 2020 | Dec 2021 | Dec 2022 | Dec 2023 | Dec 2024 | Sep 2025 | |
|---|---|---|---|---|---|---|---|---|---|---|
| Total Current Assets | 1.42B | 2.21B | 2.06B | 1.94B | 2.34B | 2.27B | 2.75B | 2.96B | 3.23B | 3.95B |
| Cash & Short-Term Investments | 789.68M | 1.4B | 1.08B | 753.81M | 1.07B | 1.01B | 1.29B | 1.07B | 1.14B | 1.56B |
| Cash Only | 408.33M | 598.03M | 493.98M | 437.45M | 649.16M | 587.28M | 724.53M | 755.13M | 942.84M | 1.31B |
| Short-Term Investments | 381.35M | 797.94M | 590.33M | 316.36M | 416.23M | 426.6M | 567.01M | 318.68M | 194.86M | 248.93M |
| Accounts Receivable | 215.28M | 261.37M | 342.63M | 377.4M | 448.35M | 373.4M | 461.32M | 633.7M | 660.53M | 908.21M |
| Days Sales Outstanding | 70.36 | 72.62 | 83.86 | 80.84 | 87.96 | 73.82 | 80.33 | 95.61 | 84.48 | - |
| Inventory | 355.13M | 475.77M | 530.87M | 680.27M | 698.55M | 776.67M | 894.08M | 1.11B | 1.23B | 1.3B |
| Days Inventory Outstanding | 618.36 | 718.23 | 614.62 | 690.75 | 486.33 | 602.5 | 648.76 | 759.54 | 775.41 | - |
| Other Current Assets | 61.71M | 74.04M | 98.4M | 130.66M | 129.93M | 110.44M | 104.52M | 141.39M | 201.53M | 185.78M |
| Total Non-Current Assets | 2.6B | 2.43B | 2.37B | 2.75B | 3.51B | 3.73B | 3.62B | 3.89B | 3.76B | 3.64B |
| Property, Plant & Equipment | 798.77M | 896.7M | 948.68M | 1.01B | 1.03B | 1.04B | 1.07B | 1.07B | 1.04B | 952.51M |
| Fixed Asset Turnover | 1.40x | 1.46x | 1.57x | 1.69x | 1.80x | 1.78x | 1.95x | 2.27x | 2.74x | - |
| Goodwill | 197.04M | 197.04M | 197.04M | 197.04M | 196.2M | 196.2M | 196.2M | 196.2M | 196.2M | 196.2M |
| Intangible Assets | 553.78M | 517.51M | 491.81M | 456.58M | 417.27M | 388.65M | 338.57M | 294.7M | 255.28M | 213.84M |
| Long-Term Investments | 572.71M | 385.79M | 235.86M | 411.98M | 285.47M | 507.79M | 333.83M | 611.13M | 521.24M | 492.24M |
| Other Non-Current Assets | 32.81M | 29.85M | 36.57M | 122.01M | 142.24M | 152.12M | 176.24M | 171.54M | 251.39M | 277.05M |
| Total Assets | 4.02B | 4.63B | 4.43B | 4.69B | 5.85B | 6B | 6.38B | 6.84B | 6.99B | 7.59B |
| Asset Turnover | 0.28x | 0.28x | 0.34x | 0.36x | 0.32x | 0.31x | 0.33x | 0.35x | 0.41x | - |
| Asset Growth % | 7.89% | 15.15% | -4.45% | 5.94% | 24.69% | 2.68% | 6.17% | 7.32% | 2.15% | 8.66% |
| Total Current Liabilities | 439.31M | 816.52M | 523.24M | 932.5M | 492.55M | 546.5M | 588.88M | 1.18B | 606.99M | 759.03M |
| Accounts Payable | 191.35M | 166.62M | 207.62M | 240.98M | 191.43M | 199.68M | 231.24M | 315.51M | 235.4M | 0 |
| Days Payables Outstanding | 333.19 | 251.52 | 240.37 | 244.69 | 133.27 | 154.9 | 167.79 | 216.44 | 148.08 | - |
| Short-Term Debt | 22.48M | 360.95M | 0 | 361.88M | 0 | 0 | 0 | 493.88M | 23.07M | 0 |
| Deferred Revenue (Current) | 0 | 0 | 1.47M | 13.04M | 152K | 6.96M | 711K | 4.62M | 1.37M | 0 |
| Other Current Liabilities | 160.57M | 208.89M | 240.07M | 202.91M | 182.82M | 258.94M | 236.1M | 234.92M | 132.06M | 759.03M |
| Current Ratio | 3.24x | 2.70x | 3.93x | 2.08x | 4.76x | 4.16x | 4.67x | 2.51x | 5.33x | 5.21x |
| Quick Ratio | 2.43x | 2.12x | 2.92x | 1.35x | 3.34x | 2.74x | 3.15x | 1.57x | 3.29x | 3.50x |
| Cash Conversion Cycle | 355.52 | 539.33 | 458.11 | 526.9 | 441.02 | 521.42 | 561.3 | 638.71 | 711.8 | - |
| Total Non-Current Liabilities | 818.11M | 1.01B | 935.95M | 635.15M | 1.25B | 1.19B | 1.18B | 713.03M | 723.96M | 747.99M |
| Long-Term Debt | 660.76M | 813.52M | 830.42M | 486.24M | 1.08B | 1.08B | 1.08B | 593.1M | 595.14M | 597.18M |
| Capital Lease Obligations | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 31.26M | 0 |
| Deferred Tax Liabilities | 0 | 44.32M | 62.07M | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Other Non-Current Liabilities | 157.34M | 194.42M | 105.53M | 148.92M | 174.32M | 113.53M | 100.02M | 119.94M | 97.57M | 150.82M |
| Total Liabilities | 1.26B | 1.82B | 1.46B | 1.57B | 1.74B | 1.74B | 1.77B | 1.89B | 1.33B | 1.51B |
| Total Debt | 683.24M | 1.17B | 830.42M | 858.82M | 1.09B | 1.09B | 1.09B | 1.1B | 649.47M | 597.18M |
| Net Debt | 274.91M | 576.44M | 336.44M | 421.37M | 437.74M | 502.26M | 368.86M | 340.62M | -293.38M | -714.5M |
| Debt / Equity | 0.25x | 0.42x | 0.28x | 0.28x | 0.26x | 0.26x | 0.24x | 0.22x | 0.11x | 0.10x |
| Debt / EBITDA | - | 16.05x | - | 177.33x | 17.61x | 42.40x | 4.16x | 3.78x | 1.12x | - |
| Net Debt / EBITDA | - | 7.88x | - | 87.01x | 7.09x | 19.54x | 1.40x | 1.17x | -0.51x | - |
| Interest Coverage | -20.34x | -0.34x | -2.83x | -4.28x | -1.48x | -5.37x | 10.08x | 10.72x | 38.23x | - |
| Total Equity | 2.77B | 2.81B | 2.97B | 3.12B | 4.11B | 4.27B | 4.6B | 4.95B | 5.66B | 6.09B |
| Equity Growth % | 15.22% | 1.53% | 5.67% | 5.2% | 31.5% | 3.89% | 7.91% | 7.57% | 14.27% | 7.58% |
| Book Value per Share | 16.64 | 16.10 | 16.74 | 17.44 | 21.42 | 23.33 | 24.36 | 25.84 | 28.76 | 31.76 |
| Total Shareholders' Equity | 2.77B | 2.81B | 2.97B | 3.12B | 4.11B | 4.27B | 4.6B | 4.95B | 5.66B | 6.09B |
| Common Stock | 173K | 176K | 178K | 180K | 182K | 184K | 186K | 189K | 191K | -10.32M |
| Retained Earnings | -1.52B | -1.64B | -1.69B | -1.72B | -861.61M | -930.76M | -789.2M | -621.55M | -194.69M | 154.21M |
| Treasury Stock | -14.32M | -14.22M | -13.3M | -9.96M | -9.84M | 0 | 0 | 0 | 0 | 0 |
| Accumulated OCI | 12.82M | -22.96M | 5.27M | 20.16M | -16.14M | 14.43M | -3.87M | -28.79M | 61.65M | -13.47M |
| Minority Interest | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Dec 2016 | Dec 2017 | Dec 2018 | Dec 2019 | Dec 2020 | Dec 2021 | Dec 2022 | Dec 2023 | Dec 2024 | Sep 2025 | |
|---|---|---|---|---|---|---|---|---|---|---|
| Cash from Operations | -227.84M | -8.76M | 20.21M | 48.26M | 85.36M | 304.54M | 175.9M | 159.26M | 572.84M | 827.99M |
| Operating CF Margin % | -20.4% | -0.67% | 1.36% | 2.83% | 4.59% | 16.49% | 8.39% | 6.58% | 20.07% | - |
| Operating CF Growth % | -2.77% | 96.16% | 330.76% | 138.83% | 76.88% | 256.75% | -42.24% | -9.46% | 259.69% | 44.54% |
| Net Income | -630.21M | -117.04M | -77.21M | -23.85M | 859.1M | -64.08M | 141.56M | 167.65M | 426.86M | 348.9M |
| Depreciation & Amortization | 96.91M | 87.86M | 95.67M | 105.3M | 105.17M | 108.04M | 101.97M | 104.39M | 96.43M | 79.56M |
| Stock-Based Compensation | 134.64M | 140.26M | 148.82M | 159.87M | 189.71M | 197.26M | 196.31M | 207.1M | 201.57M | 181.41M |
| Deferred Taxes | -228.05M | 44.46M | -68.38M | -82.76M | -888.91M | -15.61M | -52.09M | -44.98M | 56.1M | 48.74M |
| Other Non-Cash Items | 559.15M | -70.34M | -29.27M | -9.2M | 44.71M | 12.89M | -115.47M | 61.65M | 8.29M | 278.07M |
| Working Capital Changes | -160.28M | -93.96M | -49.42M | -101.09M | -224.42M | 66.03M | -96.38M | -336.54M | -216.4M | -108.68M |
| Change in Receivables | -51.48M | -25.26M | -54.27M | -37.85M | -59.03M | 65.57M | -82.03M | -190.44M | -57.91M | -228.05M |
| Change in Inventory | -64.51M | -96.89M | -23.75M | -107.55M | -61.15M | -35.06M | -68.26M | -157.06M | -63.53M | 119.21M |
| Change in Payables | -33.89M | 24.83M | 20.62M | 77.09M | -68.71M | 15.69M | 59.02M | 68.85M | -32.24M | 66.14M |
| Cash from Investing | -484.05M | -305.46M | 264.35M | -31.03M | -53.62M | -366.31M | -20.03M | -111.24M | 136.49M | -414.24M |
| Capital Expenditures | -148.38M | -199.22M | -144.62M | -163.41M | -137.52M | -95.58M | -131.54M | -107.61M | -85.42M | -103.04M |
| CapEx % of Revenue | 13.29% | 15.17% | 9.7% | 9.59% | 7.39% | 5.18% | 6.28% | 4.45% | 2.99% | - |
| Acquisitions | -2.79M | 125M | 50M | 0 | -23.21M | 0 | 0 | 0 | 0 | -285.19M |
| Investments | - | - | - | - | - | - | - | - | - | - |
| Other Investing | -698K | -1.75M | -10K | 24.19M | 89.64M | -24.64M | 103.33M | 0 | -853K | -7.94M |
| Cash from Financing | 727.11M | 507.14M | -388.01M | -74.67M | 181.12M | -48K | -18.65M | -18.73M | -526.45M | -42.39M |
| Debt Issued (Net) | 0 | 481.69M | -374.95M | -5.09M | 203.84M | -3.04M | -2.6M | -2.29M | -494.99M | 0 |
| Equity Issued (Net) | 1000K | 0 | 0 | 1000K | -1000K | 0 | 1000K | 1000K | 0 | 0 |
| Dividends Paid | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 | 0 |
| Share Repurchases | 0 | -33.51M | -35.92M | 0 | -50M | 0 | 0 | 0 | 0 | 0 |
| Other Financing | 14.17M | 25.46M | -13.05M | -101.2M | 27.27M | 2.99M | -85.38M | -85.79M | -31.46M | -42.39M |
| Net Change in Cash | 11.29M | 189.7M | -104.05M | -56.54M | 211.71M | -61.88M | 137.25M | 30.6M | 187.72M | 368.84M |
| Free Cash Flow | -376.22M | -207.98M | -124.41M | -96.76M | -52.15M | 185.31M | 54.94M | 62.57M | 475.42M | 724.96M |
| FCF Margin % | -33.69% | -15.83% | -8.34% | -5.68% | -2.8% | 10.04% | 2.62% | 2.59% | 16.66% | - |
| FCF Growth % | 16.27% | 44.72% | 40.18% | 22.22% | 46.1% | 455.31% | -70.35% | 13.88% | 659.85% | 52.49% |
| FCF per Share | -2.26 | -1.19 | -0.70 | -0.54 | -0.27 | 1.01 | 0.29 | 0.33 | 2.42 | 3.78 |
| FCF Conversion (FCF/Net Income) | 0.36x | 0.07x | -0.26x | -2.02x | 0.10x | -4.75x | 1.24x | 0.95x | 1.34x | 30.91x |
| Interest Paid | 8.64M | 8.54M | 11.62M | 0 | 12.18M | 10.39M | 0 | 0 | 10.36M | 0 |
| Taxes Paid | 95.86M | 23.89M | 16.68M | 0 | 8.98M | 18.15M | 0 | 0 | 57.27M | 0 |
| Metric | 2016 | 2017 | 2018 | 2019 | 2020 | 2021 | 2022 | 2023 | 2024 | 2025 |
|---|---|---|---|---|---|---|---|---|---|---|
| Return on Equity (ROE) | -24.39% | -4.2% | -2.67% | -0.78% | 23.63% | -1.53% | 3.19% | 3.51% | 8.05% | 0.46% |
| Return on Invested Capital (ROIC) | -21.12% | -0.34% | -2.77% | -2.2% | -0.81% | -1.33% | 2.48% | 2.71% | 6.82% | - |
| Gross Margin | 81.23% | 81.59% | 78.86% | 78.91% | 71.82% | 74.52% | 76% | 78.01% | 79.67% | - |
| Net Margin | -56.43% | -8.91% | -5.18% | -1.4% | 45.9% | -3.47% | 6.75% | 6.93% | 14.96% | - |
| Debt / Equity | 0.25x | 0.42x | 0.28x | 0.28x | 0.26x | 0.26x | 0.24x | 0.22x | 0.11x | 0.10x |
| Interest Coverage | -20.34x | -0.34x | -2.83x | -4.28x | -1.48x | -5.37x | 10.08x | 10.72x | 38.23x | - |
| FCF Conversion | 0.36x | 0.07x | -0.26x | -2.02x | 0.10x | -4.75x | 1.24x | 0.95x | 1.34x | 30.91x |
| Revenue Growth | 25.5% | 17.62% | 13.52% | 14.27% | 9.18% | -0.76% | 13.53% | 15.42% | 17.97% | -100% |
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